Idursulfase Extends Survival by a Decade in Mucopolysaccharidosis II: Final Results from the 18-Year Hunter Outcome Survey

Highlights

Patients treated with idursulfase demonstrated a median increase in survival time of approximately 10 years compared with an unmatched cohort of untreated patients.

Long-term enzyme replacement therapy (ERT) was associated with a 57.9% lower risk of death.

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